The Journal of Pediatrics
Volume 154, Issue 1 , Pages 135-139, January 2009

Use of Enzyme Replacement Therapy (Laronidase) before Hematopoietic Stem Cell Transplantation for Mucopolysaccharidosis I: Experience in 18 Patients

  • Robert F. Wynn, MD

      Affiliations

    • Blood and Marrow Transplant Unit, Royal Manchester Children's Hospital, Manchester, UK
    • Corresponding Author InformationReprint requests: Dr Robert F. Wynn, BMTU Programme Director, Royal Manchester Children's Hospital, Manchester M27 4HA, UK
    • ,
  • Jean Mercer, RGN

      Affiliations

    • Willink Unit for Biochemical Genetics, Royal Manchester Children's Hospital, Manchester, UK
    • ,
  • Joanne Page, BSc

      Affiliations

    • Blood and Marrow Transplant Unit, Royal Manchester Children's Hospital, Manchester, UK
    • ,
  • Trevor F. Carr, PhD

      Affiliations

    • Blood and Marrow Transplant Unit, Royal Manchester Children's Hospital, Manchester, UK
    • ,
  • Simon Jones, MRCPCH

      Affiliations

    • Willink Unit for Biochemical Genetics, Royal Manchester Children's Hospital, Manchester, UK
    • ,
  • J. Edmond Wraith, FRCPCH

      Affiliations

    • Willink Unit for Biochemical Genetics, Royal Manchester Children's Hospital, Manchester, UK

Received 11 February 2008; received in revised form 16 June 2008; accepted 2 July 2008.

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 Dr Wraith has undertaken paid and unpaid consultancy work for, and has been a principle investigator in, studies sponsored by Genzyme.

PII: S0022-3476(08)00577-5

doi:10.1016/j.jpeds.2008.07.004

The Journal of Pediatrics
Volume 154, Issue 1 , Pages 135-139, January 2009

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